Webinars
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Date: March 12, 2026
Time: 12-1pm EDT / 5-6pm CET
Title: Neonatal Delivery of Exon Skipping Therapeutics Maximizes Brain Dystrophin Rescue in the Mdx52 Mouse Model of DMD
Description:
In this webinar, I will explore how early-life exon-skipping strategies can be leveraged to target the brain in Duchenne muscular dystrophy. Using the mdx52 mouse model, we investigated different therapeutic tools and delivery routes to understand how timing shapes CNS engagement. This talk will highlight why the neonatal window may offer unique opportunities for enhancing brain-targeted therapies and improving future neurocognitive outcomes.
