CRISPR Therapy Reduces HAE Attacks After a Single Infusion in Phase 3
Hereditary angioedema (HAE) is a rare genetic disease that causes severe and unpredictable swelling attacks due to an overproduction of bradykinin. These attacks often affect the face, airways, abdomen, and extremities and can be life-threatening. Normally, bradykinin is produced through a process called the ...
2026 Paper of the Year Awards – Late Discovery Category
Olezarsen for Managing Severe Hypertriglyceridemia and Pancreatitis Risk https://www.nejm.org/doi/10.1056/NEJMoa2512761 Dr. Nicholas Marsten TIMI Study Group, Brigham and Women's Hospital
2026 Paper of the Year Awards – Basic Research Category
A multiobjective AI model for LNP engineering enhances tissue-selective mRNA delivery https://www.nature.com/articles/s41587-026-03109-0 Dr. Muye Zhou University of Toronto
2026 Travel Grant Awardees
Fien Aben, University of Antwerp Rosemarie Elloisa Acero, Texas A&M University Yutaro Asami, Boston Children's Hospital Celine Baron, Ludwig-Maximilians-University Munich Brianna Bramato, UMass Chan Medical School Benjamin Chang, UMass Chan Medical School Zhi Ming Cheng, UMass Chan Medical School Laura Colar Zanjko, Biotalentum Ltd. Caitlyn ...
2026 Poster Awards
Yutaro Asami Austin Brent Benjamin Chang David Cooper Caitlyn Czinder Christopher Dahlke Mojtaba Dayyani Didem Demirbas Natalie Fischhaber Katherine Gross Anders Knudsen Shirley Lee Junlang Li Xiaoge Liang Rachael Miller Christopher Oetheimer Sonya Ostashevskaya-Gohstand Mohamad Omar Rachid Emmanuel Sasu Sebastian Sjöström Christiana Wang ...
2026 Lifetime Achievement Award – John J. Rossi, PhD
John J. Rossi, Ph.D. ​ Dr. Rossi has had a more than forty year career focusing on the development of nucleic acid-based therapies and RNA interference approaches for the treatment of AIDS, cancer, and other major diseases. He is considered a world leader in ...
2026 Lifetime Achievement Award – Pieter R. Cullis, PhD
Pieter R. Cullis, Ph.D. ​ Pieter R. Cullis, Professor, Department of Biochemistry and Molecular Biology, University of British Columbia. Dr. Cullis and co-workers have been responsible for fundamental advances in the development of nanomedicines employing lipid nanoparticle (LNP) technology for cancer therapies, gene therapies ...
2026-Award for Patient Advocacy
Tim Yu, MD, PhD Boston Children's Hospital and Harvard Medical School Talk Title: Interventional genetics: who’s in the waiting room? Dr. Yu is a neurogeneticist at Boston Children’s Hospital and Harvard Medical School. He obtained his undergraduate degree in Biochemistry at Harvard College. As ...
2026 Dr. Fritz Eckstein Mid-Career Award
Daniel J. Siegwart, PhD University of Texas Southwestern Medical Center Talk Title: Development of SORT lipid nanoparticles (LNPs) for genome correction of disease-causing mutations Daniel J. Siegwart is a Professor in the Department of Biomedical Engineering at the University of Texas Southwestern Medical Center. ...
2026 Nucleic Acid Therapeutics Journal Young Investigator Award
Sonia Vallabh, PhD Eric Minikel, PhD The Broad Institute Talk title: Advancing oligonucleotide therapeutics for prion disease Sonia Vallabh and Eric Minikel are a wife-husband team who co-run a prion disease research laboratory at the Broad Institute of MIT and Harvard. Their work is ...
