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Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease
Zeitler B, Froelich S, Marlen K, Shivak DA, Yu Q, Li D, Pearl JR, Miller JC, Zhang L, Paschon DE, Hinkley SJ, Ankoudinova I, Lam S, Guschin D, Kopan L, Cherone JM, Nguyen HB, Qiao G, Ataei Y, Mendel MC, …
July 31, 2019
Enhancing gene editing specificity by attenuating DNA cleavage kinetics
Miller JC, Patil DP, Xia DF, Paine CB, Fauser F, Richards HW, Shivak DA, Bendaña YR, Hinkley SJ, Scarlott NA, Lam SC, Reik A, Zhou Y, Paschon DE, Li P, Wangzor T, Lee G, Zhang L, Rebar EJ. Nat Biotechnol. …
Short-Acting Anti-VWF (von Willebrand Factor) Aptamer Improves the Recovery, Survival, and Hemostatic Functions of Refrigerated Platelets
Chen W, Voos KM, Josephson CD, Li R. Arterioscler Thromb Vasc Biol. 2019 Jul 18 PubMed
The Arsenic Binding Aptamer Cannot Bind Arsenic: Critical Evaluation of Aptamer Selection and Binding
Zong C, Liu J. Anal Chem. 2019 Jul 25. PubMed
Assay Determination by Mass Spectrometry for Oligonucleotide Therapeutics
Madsen M, Roussis S, Schniepp E, Rentel C, Capaldi D. Rapid Commun Mass Spectrom. 2019 Jul 6. PubMed
Page 85 of 212
Page 85 of 212
Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease
Zeitler B, Froelich S, Marlen K, Shivak DA, Yu Q, Li D, Pearl JR, Miller JC, Zhang L, Paschon DE, Hinkley SJ, Ankoudinova I, Lam S, Guschin D, Kopan L, Cherone JM, Nguyen HB, Qiao G, Ataei Y, Mendel MC, …
Enhancing gene editing specificity by attenuating DNA cleavage kinetics
Miller JC, Patil DP, Xia DF, Paine CB, Fauser F, Richards HW, Shivak DA, Bendaña YR, Hinkley SJ, Scarlott NA, Lam SC, Reik A, Zhou Y, Paschon DE, Li P, Wangzor T, Lee G, Zhang L, Rebar EJ. Nat Biotechnol. …
Short-Acting Anti-VWF (von Willebrand Factor) Aptamer Improves the Recovery, Survival, and Hemostatic Functions of Refrigerated Platelets
Chen W, Voos KM, Josephson CD, Li R. Arterioscler Thromb Vasc Biol. 2019 Jul 18 PubMed
The Arsenic Binding Aptamer Cannot Bind Arsenic: Critical Evaluation of Aptamer Selection and Binding
Zong C, Liu J. Anal Chem. 2019 Jul 25. PubMed
Assay Determination by Mass Spectrometry for Oligonucleotide Therapeutics
Madsen M, Roussis S, Schniepp E, Rentel C, Capaldi D. Rapid Commun Mass Spectrom. 2019 Jul 6. PubMed
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