• Category

Found 1056 Results
Page 85 of 212

Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease


Zeitler B, Froelich S, Marlen K, Shivak DA, Yu Q, Li D, Pearl JR, Miller JC, Zhang L, Paschon DE, Hinkley SJ, Ankoudinova I, Lam S, Guschin D, Kopan L, Cherone JM, Nguyen HB, Qiao G, Ataei Y, Mendel MC, …

July 31, 2019


Enhancing gene editing specificity by attenuating DNA cleavage kinetics


Miller JC, Patil DP, Xia DF, Paine CB, Fauser F, Richards HW, Shivak DA, Bendaña YR, Hinkley SJ, Scarlott NA, Lam SC, Reik A, Zhou Y, Paschon DE, Li P, Wangzor T, Lee G, Zhang L, Rebar EJ. Nat Biotechnol. …




Assay Determination by Mass Spectrometry for Oligonucleotide Therapeutics


Madsen M, Roussis S, Schniepp E, Rentel C, Capaldi D. Rapid Commun Mass Spectrom. 2019 Jul 6. PubMed


Page 85 of 212
  • Category

Found 1056 Results
Page 85 of 212

Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease


Zeitler B, Froelich S, Marlen K, Shivak DA, Yu Q, Li D, Pearl JR, Miller JC, Zhang L, Paschon DE, Hinkley SJ, Ankoudinova I, Lam S, Guschin D, Kopan L, Cherone JM, Nguyen HB, Qiao G, Ataei Y, Mendel MC, …


Enhancing gene editing specificity by attenuating DNA cleavage kinetics


Miller JC, Patil DP, Xia DF, Paine CB, Fauser F, Richards HW, Shivak DA, Bendaña YR, Hinkley SJ, Scarlott NA, Lam SC, Reik A, Zhou Y, Paschon DE, Li P, Wangzor T, Lee G, Zhang L, Rebar EJ. Nat Biotechnol. …




Assay Determination by Mass Spectrometry for Oligonucleotide Therapeutics


Madsen M, Roussis S, Schniepp E, Rentel C, Capaldi D. Rapid Commun Mass Spectrom. 2019 Jul 6. PubMed


Page 85 of 212