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Steric Inhibition of 5′ UTR Regulatory Elements Results in Upregulation of Human CFTR
Sasaki S, Sun R, Bui HH, Crosby JR, Monia BP, Guo S. Mol Ther. 2019 Jul 12. pii: S1525-0016(19)30312-0. PubMed
July 31, 2019
Antisense oligonucleotides extend survival of prion-infected mice
Raymond GJ, Zhao HT, Race B, Raymond LD, Williams K, Swayze EE, Graffam S, Le J, Caron T, Stathopoulos J, O’Keefe R, Lubke LL, Reidenbach AG, Kraus A, Schreiber SL, Mazur C, Cabin DE, Carroll JB, Minikel EV, Kordasiewicz H, …
LncRNA HAND2-AS1 promotes liver cancer stem cell self-renewal via BMP signaling
Wang Y, Zhu P, Luo J, Wang J, Liu Z, Wu W, Du Y, Ye B, Wang D, He L, Ren W, Wang J, Sun X, Chen R, Tian Y, Fan Z. EMBO J. 2019 Jul 23:e101110. PubMed
AGO CLIP Reveals an Activated Network for Acute Regulation of Brain Glutamate Homeostasis in Ischemic Stroke
Kobayashi M, Benakis C, Anderson C, Moore MJ, Poon C, Uekawa K, Dyke JP, Fak JJ, Mele A, Park CY, Zhou P, Anrather J, Iadecola C, Darnell RB. Cell Rep. 2019 Jul 23;28(4):979-991.e6. PubMed
Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease
Zeitler B, Froelich S, Marlen K, Shivak DA, Yu Q, Li D, Pearl JR, Miller JC, Zhang L, Paschon DE, Hinkley SJ, Ankoudinova I, Lam S, Guschin D, Kopan L, Cherone JM, Nguyen HB, Qiao G, Ataei Y, Mendel MC, …
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