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Safety and Efficacy of the BNT162b2 mRNA Covid-19 Vaccine
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Ligand conjugated antisense oligonucleotide for the treatment of transthyretin amyloidosis: preclinical and phase 1 data
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Post-Transcriptional Genetic Silencing of BCL11A to Treat Sickle Cell Disease
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Double Controlled Release of Therapeutic RNA Modules through Injectable DNA-RNA Hybrid Hydrogel
Han S, Park Y, Kim H, Nam H, Ko O, Lee JB. ACS Appl Mater Interfaces. 2020 Dec 16;12(50):55554-55563. Pubmed
Exosome-mediated delivery of antisense oligonucleotides targeting α-synuclein ameliorates the pathology in a mouse model of Parkinson’s disease
Yang J, Luo S, Zhang J, Yu T, Fu Z, Zheng Y, Xu X, Liu C, Fan M, Zhang Z. Neurobiol Dis. Epub 2020 Dec 6. Pubmed
Docosanoic acid conjugation to siRNA enables functional and safe delivery to skeletal and cardiac muscles
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MOTS-c promotes phosphorodiamidate morpholino oligomer uptake and efficacy in dystrophic mice
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DNA Polymerase Variants with High Processivity and Accuracy for Encoding and Decoding Locked Nucleic Acid Sequences
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