Muscle targeted siRNA Conjugates for Pompe Disease
Time: 8AM PST / 11AM EST / 5PM CET Date: August 3, 2023 Aro Biotx is focused on developing Centyrin-siRNA conjugates for treatment of extrahepatic genetic diseases. Our lead program employs a CD71 Centyrin for targeting to muscle together with an siRNA for ...
Developing Oligonucleotides Into Therapies: Opportunities and Challenges
Time: 8AM PST / 11AM EST / 5PM CET Date: July 6, 2023 Speakers: Shalini Andersson, PhD Vice President of Oligonucleotide Discovery AstraZeneca View Bio
Pathways for patient-centered interventional genomic medicine
Time: 8AM PST | 11AM EST | 5PM CET Date: June 22, 2023 Speakers: Timothy Yu, PhD, MD Neurogeneticist Boston Children’s Hospital and Harvard Medical School View Bio
Introduction to Nucleic Acid Immunity, and It’s Implications For Optimizing Cancer Immunotherapy
Time: 8AM PST | 11AM EST | 5PM CET Date: June 8, 2023 Starting from the concept and principles of Nucleic Acid Immunity, I will explain why TLR7 and TLR9 are unique among the nucleic acid immune sensing receptors for their ability to ...
Trainee Spotlight Series: Remko Goossens & Priyanka Shukla
Time: 8AM Pacific | 11AM Eastern | 5PM CET Date: May 18, 2023 Speakers: Remko Goossens Leiden University Medical Center Remko will outline our findings concerning the relationship between the splicing speed of ...
Realizing the Promise of CRISPR Therapeutics: In Vivo and Cell Therapy Applications
Time: 8am Pacific | 11am Eastern | 5pm CET Date: May 11, 2023 Laura will be discussing preclinical and clinical data for CRISPR based investigational drug candidates from Intellia Therapeutics. Speakers: Laura Sepp-Lorenzino, ...
The World of GalNAc-Conjugates in Nucleic Acid Therapeutics
Time: 5pm Amsterdam - 9 AM MST Date: April 27, 2023 Speakers: Mano Manoharan, PhD View Bio
Trainee Spotlight Series: Jeremy Hall and Tracy Mallette
Time: 5pm Amsterdam Date: April 13, 2023 Topics/Speakers: Oligo-PROTAC strategy for cell-selective and targeted degradation of activated STAT3 Jeremy Hall City of Hope & Keck Graduate Institute Jeremy will present a summary of the ...
Trainee Spotlight Series: OTS 2022 poster winners
Time: 05:00 PM - Amsterdam, Berlin, Rome, Stockholm, Vienna Date: March 30, 2023 Topics/Speakers: Therapeutic application of engineered U1 snRNAs in retinopathies and other disorders Paolo Pigini Assessing efficacy ...
Spotting Stubborn Indirect Effects in Oligonucleotide Therapeutics
Time: 4pm CET Date: March 16, 2023 We use chemistry to improve the properties of nucleic acid therapeutics including antisense oligonucleotides, siRNAs, and genome editing approaches. I will walk through a recent study we carried out trying to activate frataxin expression to treat ...
