Financing the Future of Individualized Medicine: Funding Models for Rare Genetic Therapies
Date: September 18, 2025 Time: 11-12pm EDT / 5-6pm CEST Title:Financing the Future of Individualized Medicine: Funding Models for Rare Genetic Therapies Description: Individualized medicine has emerged as an approach offering bespoke therapeutics to patients with rare genetic conditions. In spite ...
From Discovery to Deals: The Neurological Oligonucleotide Landscape at a Glance
Date: September 4, 2025 Time: 11-12pm EDT / 5-6pm CEST Title: From Discovery to Deals: The Neurological Oligonucleotide Landscape at a Glance Description: A deep dive on the drug landscape, displaying critical data-driven therapeutic and clinical trial highlights, as well as ...
Behind the Rapid Development of an Individualized CRISPR Therapy for a Deadly Rare Disease
A baby is the first person to receive a bespoke CRISPR therapy designed specifically for him that directly fixes a disease-causing mutation in his genome. It wasn't long after KJ was born in the summer of 2024 that doctors noticed something was wrong. Within ...
2024 OTS Travel Grant Recipients
Muna Abedrabbo, The University of British ColumbiaUnnur J. Björgvinsdóttir, Technical University of DenmarkMathilde Blitek, U1179 UVSQRut Bryl, UT Southwestern Medical CenterJessica Cale, PhD, Centre for Molecular Medicine and Innovative TherapeuticsMyriam Cerezo-Magaña, PhD, Lund UniversityDavid Cheerie, The Hospital for Sick ChildrenMarguerite Colin, MRC Toxicology Unit, University ...
2024 Patient Advocacy Award
Katie Gross Research Associate, RNA Therapeutics Institute, UMASS Chan Medical School Biography Katie Gross is a Research Associate in the laboratory of Dr. Julia Alterman and Dr. Anastasia Khvorova in the RNA Therapeutics Institute at the University of Massachusetts Chan Medical School. She began ...
2024 Dr. Alan M. Gewirtz Memorial Scholarship – Graduate Students
Jillian Belgrad, M.D./Ph.D. Candidate, MS3/GS4 Khvorova Lab, RNA Therapeutics Institute, UMass Chan Medical School  Biography: Jillian Belgrad is a sixth-year MD/PhD student in the RNA Therapeutics Institute at UMass Chan Medical School. Before joining UMass Chan, Jillian graduated from Colgate University with a ...
2024 Dr. Alan M. Gewirtz Memorial Scholarship – Postdoctoral Fellows and Junior Industrial Professionals
Hassan H. Fakih, Ph.D. Post-Doctoral Associate, Prof. Anastasia Khvorova Research Group RNA Therapeutics Institute | UMASS Chan Medical School Biography: Hassan is a Postdoctoral Associate in the lab of Prof. Anastasia Khvorova at the RNA Therapeutics Institute at UMass Chan Medical School. His research focuses on ...
2024 Mary Ann Liebert Publishers Inc., Young Investigator Award
Hélène Tran, Ph.D. Research Director, Head of Antisense Oligonucleotide Therapeutics, Neurology Therapeutic Area, Servier Research Institute, France Biography: Hélène Tran is a Director in the Neuroscience Therapeutic Area at the Servier Research & Development Institute in Paris-Saclay, where she leads the antisense oligonucleotide (ASO) therapeutics ...
2024 Paper of the Year – Basic Research category
Dr. Mikyung Yu, Ph.D. Alnylam Pharmaceuticals Evaluating the oral delivery of GalNAc-conjugated siRNAs in rodents and non-human primates 2024 Paper of the Year – Basic Research category https://pubmed.ncbi.nlm.nih.gov/38742636/ Biography: Mikyung Yu, Ph.D., is a Principal Scientist in Research at Alnylam Pharmaceuticals. Dr. Yu led the ...
The Oligonucleotide Therapeutics Society Announces the 21st Annual Meeting in Budapest, Hungary
The Oligonucleotide Therapeutics Society (OTS) is pleased to announce the 21st Annual OTS Meeting, scheduled for October 19–22, 2025, at the Budapest Congress Center in Budapest, Hungary. This premier global gathering of the oligonucleotide community is renowned for fostering dynamic, cross-disciplinary dialogue—bringing together leaders ...
