MicroRNA-221 Is Cardioprotective and Anti-fibrotic in a Rat Model of Myocardial Infarction
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Discovery and preclinical evaluation of anti-miR-17 oligonucleotide RGLS4326 for the treatment of polycystic kidney disease
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Combining Engineered U1 snRNA and Antisense Oligonucleotides to Improve the Treatment of a BBS1 Splice Site Mutation
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Suppression of Mutant Protein Expression in SCA3 and SCA1 Mice Using a CAG Repeat-Targeting Antisense Oligonucleotide
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CRISPR-Cas9-based mutagenesis frequently provokes on-target mRNA misregulation
Tuladhar R, Yeu Y, Tyler Piazza J, Tan Z, Rene Clemenceau J, Wu X, Barrett Q, Herbert J, Mathews DH, Kim J, Hyun Hwang T, Lum L. Nat Commun. 2019 Sep 6;10(1):4056. PubMed
CRISPR DNA base editors with reduced RNA off-target and self-editing activities
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Click-Particle Display for Base-Modified Aptamer Discovery
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Massively parallel RNA device engineering in mammalian cells with RNA-Seq
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An in Vivo miRNA Delivery System for Restoring Infarcted Myocardium
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Peptide-conjugated oligonucleotides evoke long-lasting myotonic dystrophy correction in patient-derived cells and mice
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