2023 Mary Ann Liebert Publishers, Inc. Young Investigator Award Winner Bahal Raman, PhD
Bahal Raman, PhD University of Connecticut
2023 Dr. Alan M. Gewirtz Memorial Scholarship – For Graduate Students Winner Krystal Johnson, PhD
Krystal Johnson, PhD UT Southwestern Medical Center Biography: Krystal joined David Corey’s Lab at UT Southwestern Medical Center (UTSW) to pursue her Ph.D. in 2018 after finishing her B.S. in Biochemistry at UT Austin. She was awarded a NIGMS F31 Diversity Fellowship for her ...
2023 Dr. Alan M. Gewirtz Memorial Scholarship – Postdoctoral Fellows and Junior Industrial Professionals Winner Dan O’Reilly, PhD
Ronald Buijsen, PhD Leiden University Medical Center Biography: Dr. Buijsen has expertise in antisense oligonucleotide (AON) design and optimization in cell models and animal models using a wide variety of molecular, immunohistochemical and
2023 Award for Science Outreach Winner Julia Vitarello
Julia Vitarello Mila’s Mom | Mila’s Miracle Foundation
2023 Paper of the Year Award – Late Discovery Category Winner Jinkuk Kim, PhD
Jinkuk Kim, PhD KAIST - Korea Advanced Institute of Science and Technology A framework for individualized splice-switching oligonucleotide therapy https://pubmed.ncbi.nlm.nih.gov/37438524/ Biography: Jinkuk Kim is an Assistant Professor at KAIST in South Korea. He obtained a B.S. in computer science and a Ph.D. ...
2023 Annual Meeting Highlights
We are pleased to note that this year’s annual Oligonucleotide Therapeutics Society meeting in Barcelona, Spain had the highest involvement of any previous meeting, with 800 in-person attendees, 297 abstract submissions, 260 posters, 47 travel grants, 36 Sponsors, and 29 Exhibitors. We hope all ...
Fanzor: A Programmable RNA-Guided System In Eukaryotes Similar to CRISPR
Researchers have uncovered the first programmable RNA-guided system in eukaryotes that could be even more precise than CRISPR gene-editing. The discovery — led by Feng Zhang at the McGovern Institute for Brain Research at MIT and the Broad Institute of MIT and Harvard — demonstrates ...
RNAi: The Persistence of a Few Leads to Success
On August 10, 2018, the U.S. Food and Drug Administration (FDA) approved the first RNAi therapy. The approval marked a significant milestone not just for the drug but the entire field of RNA interference (RNAi). The success of the technology was never guaranteed, and ...
From Failure to Meet the Clinical Endpoint to U.S. Food and Drug Administration Approval: 15th Antisense Oligonucleotide Therapy Approved Qalsody (Tofersen) for Treatment of SOD1 Mutated Amyotrophic Lateral Sclerosis
On April 25 2023, the U.S. Food and Drug Administration (FDA) granted accelerated approval to tofersen (trade name Qalsody) for the treatment of Superoxide Dismutase 1 (SOD1) associated amyotrophic lateral sclerosis (ALS) [1]. The clinical trial failed to meet its primary endpoint; however, approval ...
